For children born with severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID), an investigational ...
News Medical on MSN
Gene therapy shows long-term success in children with rare immune disorder
Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the ...
A new gene therapy approach aimed at protecting people with type 1 diabetes from developing diabetic kidney disease—a serious ...
In February, the biotech reported improvements in 10 of 11 children who received DB-OTO. The AAV gene therapy, which ...
University of Bristol researchers have discovered a VEGF-C gene therapy that protects the kidneys in people with type 1 diabetes ...
In May, a historic moment in science and medicine was captured in a single photo that circulated across news outlets ...
In a preclinical mouse study, gene therapy delivering VEGFC to kidney cells reduced early signs of kidney damage in Type 1 ...
The neurodegenerative disease damages patients’ motor, cognitive and behavioral controls, which sometimes manifest as ...
FOX 9 Minneapolis-St. Paul on MSN
Coon Rapids family fights rare genetic disease to save daughter's life
As their 8-month-old daughter prepares for gene therapy treatment, a Coon Rapids family is bracing for three months of ...
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